Fortuity Pharma

Bringing Affordable Therapies to Rare Disease Communities.

About Fortuity Pharma

Fortuity Pharma is a public-benefit corporation dedicated to developing effective and affordable therapies for rare diseases.

By repurposing existing drugs and nutraceuticals, we aim to address unmet medical needs in the rare disease community. Our lead effort involves bringing the drug amlexanox back to market, as it has shown promise as a readthrough therapy for genetic disorders caused by premature stop codons. Inspired by cases like Lucia’s — who saw significant improvement with amlexanox — our mission is to make therapies accessible to those who need them most.

For Patients

For Clinicians

For Investors

About Amlexanox

Our primary focus is repurposing amlexanox, an anti-inflammatory drug that has been used for a variety of conditions, including asthma and diabetes.

With a proven safety profile and low production costs, amlexanox has shown success in preclinical studies for genetic disorders like cystic fibrosis, Duchenne muscular dystrophy, Charcot-Marie-Tooth disease, Aspartylglucosaminuria, and epidermolysis bullosa. We are working towards FDA approval with orphan drug designation to ensure this treatment is available to the rare disease community at an affordable cost.

How We Help Patients

For Clinicians

Meet the Fortuity Pharma Team

Fortuity Pharma is led by a team of experienced therapy developers.

Dr. Bruce Bloom, an expert in drug repurposing, is the founder and CEO of the organization. Dr. Bloom has helped bring repurposed therapies to over a dozen rare diseases as founder and CEO of Cures Within Reach and as an executive at Healx. Dr. Clara Tang, COO of Fortuity Pharma, brings extensive operational and business development experience in rare diseases and biotech start-ups. Dr. Sitta Sittampalam is a global expert in the discovery and development of new medicines and diagnostics in pharma, academia and government. We are working with other determined and dedicated individuals to create a shared mission to make affordable treatments available to those in need.

Contact Fortuity Pharma

For Investors

Our Partners

Fortuity Pharma have partnered with experienced drug manufacturers Bright Path Labs and On Demand Pharmaceuticals to create enough amlexanox to be tested in patient cell lines. We also work in partnership with the WWOX Foundation, the COMBINEDBrain Observational Trial Working Group and other rare disease organizations, advocates, clinicians and researchers who are committed to advancing therapies like amlexanox.